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Diseases and disorders currently treatable with mainly allogeneic stem cell transplants

Haemoglobinopathies and blood disorders

Amegakaryocytic thrombocytopenia
Aplastic anaemia
Blackfan Diamond anaemia
Congenital cytopenia
Evan's syndrome
Fanconi's syndrome
Kostmann's syndrome
Thalassemia

 

Immunodeficiencies

Adrenosine deaminase deficiency
Chronic granulomatous disease
Severe combined immunodeficiency diseases
Wiskott-Aldrich syndrome
X-linked lymphoproliferative disease

Malignancies

Acute lymphocytic leukaemia
Acute myelogenous leukaemia
Acute non-lymphocytic leukaemia
Chronic lymphocytic leukaemia
Chronic myelocytic leukaemia
Ewing's tumour - sarcoma
Hodgkin's disease
Juvenile myelomonocytic leukaemia
Multiple myeloma
Myelodysplastic syndrome
Neuroblastoma
Non-Hodgkin's lymphoma

Inborn errors of metabolism

Andrenoleukodystrophy
AL amyloidosis
Bare lymphocyte syndrome
Dyskeratosis congenital
Familial erthrophagocytic lymphohistiocytosis
Gaucher's disease
Gunther's disease
Hunter's syndrome
Hurler's syndrome
Inherited neuronal ceriod lipofuscinosis
Krabbe's disease
Langerhans cell histiocytosis
Lesch-Nyhan syndrome
Leukocyte adhesion deficiency
Osteopetrosis

 
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